MIGLUSTAT is a Schedule H drug.
Miglustat reduces the formation of a certain protein in the body in people with type 1 Gaucher disease. Gaucher disease is a genetic condition in which the body lacks the enzyme needed to break down certain fatty materials (lipids). Lipids can build up in the body, causing symptoms such as easy bruising or bleeding, weakness, anemia, bone or joint pain, enlarged liver or spleen, or weakened bones that are easily fractured. Miglustat may improve the condition of the liver, spleen, bones, and blood cells in people with Type I Gaucher disease. However, miglustat is not a cure for this condition.


MIGLUSTAT is generally used to treat: Gaucher Disease Type 1

Frequently Asked Questions

Q: Is it safe on my liver?
A: Not Safe

Q: Is it safe on my kidney?
A: Check with your Doctor first

Q: Can I take it with alcohol?
A: Not Safe

Q: Is it safe for children?
A: Ask your doctor

Q: Can it be taken during pregnancy?
A: Not enough studies to prove Risk – Ask your Doctor

How Do I Take It?

Route of Administration: Oral


Caution should be exercised in patients with history of a sensation of numbness or tingling, stomach problems (e.g., inflammatory bowel disease), hand tremors, kidney impairment, who are taking other medications, any allergy, children, during pregnancy and breastfeeding. It may cause dizziness, do not drive a car or operate machinery while taking this medication. Avoid alcohol consumption. It may reduce platelet counts; avoid injury or bruising. Follow the diet and exercise program as directed by your healthcare provider.

Common Side-Effects

MIGLUSTAT : Diarrhoea, Nausea, Vomit, Abdomen Pain, Head Headache, Body Muscle Cramps Or Spasms (painful), Dizziness, Weakness (generalized), Weight Loss (unintentional)

Rare Side-Effects

MIGLUSTAT : Skin Rash, Difficulty Breathing, Face Swelling, Body Itching

Disease Interactions

MIGLUSTAT can interfere with: Inflammatory Bowel Disease, Acute Renal Failure, Thrombocytopenia

Technical Classification


Storage Conditions

Room Temperature (Between 15 To 25 C)

Available Alternatives

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